Does My Child Have Duchenne Muscular Dystrophy? Take the Quiz.
Duchenne muscular dystrophy — sometimes referred to simply as Duchenne — is a genetic disorder that causes progressive muscle loss and weakness. It occurs as a result of gene mutations involved in the production of a protein called dystrophin, according to the Muscular Dystrophy Association (MDA).
Dr. Barry Byrne Presents Improvements in Key Duchenne Muscular Dystrophy Measures, Microdystrophin Expression
Data presented by Barry Byrne, MD, Ph.D. suggest that intravenous SGT-001 (Solid Biosciences) is well-tolerated and efficacious in DMD.
Barry Byrne, MD, Ph.D.: Landscape of Awareness for Neuromuscular Disease
Barry J. Byrne, MD, Ph.D., chief medical advisor of the Muscular Dystrophy Association and associate chair of pediatrics and director at the University of Florida Powell Center for Rare Disease Research and Therapy, talked with NeurologyLive about the virtual telethon to create awareness for a number of neuromuscular diseases.
Dr. Barry Byrne Receives “See the Light” Award From the Mathew Forbes Romer Foundation
For families facing a devastating diagnosis of pediatric neurodegenerative genetic disease, Barry Byrne, M.D., Ph.D., provides a sense of hope and possibility.... Read More
Gene Therapy Company AavantiBio Launches With $107 Million Series A Financing From Perceptive Advisors, Bain Capital Life Sciences, RA Capital Management and Sarepta Therapeutics
A premier syndicate of life sciences investors including Perceptive Advisors, Bain Capital Life Sciences, and RA Capital Management, together with Sarepta Therapeutics,... Read More
University of Florida Received £500,000 Grant From Duchenne UK to Overcome Immunity Challenges in Gene Therapy
Duchenne UK has partnered with one of the world’s leading gene therapy teams focusing on AAV immunology. Drs. Manuela Corti and Barry... Read More
Adapting Neurological Care Amid COVID-19
As the ongoing battle against the spread of COVID-19 continues, the medical community is learning more about the disease and at-risk populations... Read More
Dr. Barry Byrne Featured in Denison Magazine
Barry J. Byrne, M.D., Ph.D., director of the University of Florida Powell Gene Therapy Center, a professor in Pediatrics and Molecular Genetics &... Read More
UF Health Researchers Working to Develop COVID-19 Vaccine Using Gene Therapy Technique
A team of University of Florida Health researchers is using an established gene therapy technique to quickly develop a COVID-19 vaccine that could be... Read More
