UF Health Researcher’s Gene Therapy Technique Being Further Developed to Treat Neurodegenerative Disorders
A gene therapy technique discovered by a University of Florida Health researcher and her colleague is now being used to develop treatments for neurodegenerative disorders.
During gene therapy, engineered viruses are used to deliver new genes to a patient’s cells. But in some patients, the immune system recognizes and fights the helpful adeno-associated virus, or AAV. A redesigned virus that can slip past the immune system was successfully tested in human and animal serum in 2017.