Tag

Duchenne muscular dystrophy

Solid Biosciences Shares Updates on Inspire Duchenne Clinical Trial of SGT-003

Solid Biosciences, a life sciences company developing precision genetic medicines for neuromuscular and cardiac diseases that acquired UF startup AavantiBio, shared updates on the INSPIRE DUCHENNE clinical trial for their next-generation AAV micro-dystrophin gene therapy candidate, SGT-003, for the treatment of Duchenne.

UF Team Plays Major Role in Success of Newly Approved Duchenne Muscular Dystrophy Drug

Duchenne muscular dystrophy families, advocates and healthcare providers celebrated a milestone in March with the U.S. Food and Drug Administration’s approval of the first nonsteroidal drug for the treatment of Duchenne. The University of Florida's expertise in magnetic resonance imaging provided objective, measurable results in the drug's clinical trials.