Gene Therapy Offers Hope to People With Achromatopsia, an Inherited Retinal Eye Disease

For years, people with inherited retinal diseases (IRDs), such as achromatopsia (ACHM), have been undiagnosed, misdiagnosed or delayed seeking genetic testing to confirm their diagnosis due to the lack of treatment options. Thanks to the rapid advancement of gene therapy research, this situation is changing. Achromatopsia patients, however, still face a long journey in pursuit […]

AGTC Posts Quarterly Income (Healio)

UF startup and UF Innovate | Sid Martin Biotech graduate Applied Genetic Technologies Corporation reported a net income of $1.2 million for the first quarter of its fiscal year compared with a net loss of $1.4 million in the same quarter of 2017. General and administrative expenses decreased from $3.7 million to $3.2 million, while […]

AGTC Treats First Patient of Second Cohort in Phase 1/2 Clinical XLRP Study; Earns $10 Million Enrollment Milestone (BioFlorida)

Applied Genetic Technologies Corporation, a biotechnology company conducting human clinical trials of adeno-associated virus (AAV)-based gene therapies for the treatment of rare diseases, announced that it has enrolled the first patient of the second cohort in the company’s Phase 1/2 clinical trial evaluating the safety and efficacy of an investigational AAV-based gene therapy for the […]